The outcomes of an international Phase III clinical trial conducted by researchers from the University of Pennsylvania Perelman School of Medicine and a multicenter group of investigators, published in the New England Journal of Medicine, show that adults with haemophilia B experienced an average 71% reduction in the number of […]
Clinical Trials
A novel vaccine candidate that offers protection against Lassa fever has been developed by researchers from Thomas Jefferson University and the University of Maryland Baltimore, in partnership with the Geneva Foundation and the United States Army Medical Research Institute of Infectious Diseases (USAMRIID). In preclinical animal models, the study, which […]
A Phase 1/2 trial included 15 individuals in total, among them three pediatric patients. The patients all suffered from the disease Leber congenital amaurosis caused by a gene that is essential in making proteins crucial to vision.
The rates of heart failure events and cardiovascular death were lower in the finerenone group compared with the placebo group.
Delivering a healthy copy of a gene to a person whose gene(s) are malfunctioning is known as gene therapy.
