CAR T cell therapy allows a patient’s T cells to be reprogrammed to identify and eliminate the cancer cells
CRISPR
Senior Investigator Alex Marson, MD, PhD, delved deeply into T-cell DNA to identify certain nucleotides, which are fundamental building blocks of genetic information
Casgevy, one of these treatments, is the first FDA-approved medication to make use of a revolutionary form of genome editing technique
An approval which can transform the treatment technology for β-thalassemia and sickle-cell disease